Small Nuclear RNA Base Editing: A Safer Alternative to CRISPR? Gene editing is at the forefront of medical innovation, but widespread use of CRISPR technology has raised concerns about unintended genetic changes. Researchers are now exploring small nuclear RNA (s... biotechnology CRISPR gene editing genetic therapy precision medicine RNA editing snRNA
Four Distinct Autism Subtypes Are Shaping Precision Diagnosis and Care Autism is often described as a spectrum, but a groundbreaking study is now redefining what that truly means. By analyzing data from more than 5,000 children, researchers have identified four distinct ... autism clinical research genetics neurodevelopment personalized care precision medicine subtypes
MIT Introduces Precision in Genome Editing: Anti-CRISPR Protein Delivery System A recent breakthrough by MIT and Harvard scientists is set to enhance the safety and accuracy of the widely used CRISPR-Cas9 gene-editing tool, setting the stage for more effective gene therapies. Und... anti-CRISPR biotechnology CRISPR gene therapy genome editing MIT research precision medicine protein delivery
Connectome 2.0: Brain Imaging with Ultra-High-Resolution MRI Scientists have achieved a remarkable leap in brain imaging with the introduction of the Connectome 2.0 MRI scanner. This advanced technology makes it possible to visualize the brain's intricate wirin... brain imaging BRAIN Initiative connectome MRI neurological disorders neurotechnology NIH precision medicine
Yale’s Antibody-RNA Therapy: Tackling Treatment Resistant Cancers Recent advances at Yale are reshaping the fight against some of the toughest cancers. Researchers have engineered a unique antibody-RNA therapy that offers renewed hope for patients where traditional ... antibody-RNA cancer therapy clinical trials immunotherapy precision medicine resistant tumors Yale research
Unveiling Hidden Cell Subtypes to Transform Cancer Research CellLENS is a groundbreaking artificial intelligence tool developed by a multidisciplinary team led by MIT designed to precisely identify which immune cells are fighting, helping, or hindering tumors,... artificial intelligence biomarkers cancer research cell subtypes deep learning immunotherapy precision medicine
Yale Scientists Triple Precision and Reach in Human Gene Editing Yale genome engineers are dramatically expanding the capacity and accuracy of gene editing. The work recently published in Nature , may change how we approach gene editing across research and personal... biotechnology CRISPR disease research gene editing genome engineering precision medicine Yale research
AI Powers Precision Gene Delivery Systems For Brain and Spinal Cord Therapy Thanks to innovative gene delivery systems developed by NIH-funded teams, we may soon be able to deliver genetic instructions directly and precisely to select cells within the brain or spinal cord. Th... AAV vectors brain research gene therapy neurological disorders neuroscience NIH BRAIN Initiative precision medicine
Personalized Gene Therapy: A Lifesaving Advance for Infants with Rare Diseases Picture the heartbreak of learning your newborn has a rare, life-threatening genetic disorder with no proven cure. Now, imagine that within months, a customized therapy could rewrite that child’s dest... CRISPR gene therapy infant health liver disorders NIH research precision medicine rare diseases