AI Powers Precision Gene Delivery Systems For Brain and Spinal Cord Therapy Thanks to innovative gene delivery systems developed by NIH-funded teams, we may soon be able to deliver genetic instructions directly and precisely to select cells within the brain or spinal cord. Th... AAV vectors brain research gene therapy neurological disorders neuroscience NIH BRAIN Initiative precision medicine
Personalized Gene Therapy: A Lifesaving Advance for Infants with Rare Diseases Picture the heartbreak of learning your newborn has a rare, life-threatening genetic disorder with no proven cure. Now, imagine that within months, a customized therapy could rewrite that child’s dest... CRISPR gene therapy infant health liver disorders NIH research precision medicine rare diseases