Personalized Gene Therapy: A Lifesaving Advance for Infants with Rare Diseases Picture the heartbreak of learning your newborn has a rare, life-threatening genetic disorder with no proven cure. Now, imagine that within months, a customized therapy could rewrite that child’s dest... CRISPR gene therapy infant health liver disorders NIH research precision medicine rare diseases
How evoCAST Is Transforming Precision Gene Editing Having the power to insert entire genes precisely where you want in the human genome is the remarkable promise of evoCAST , the latest innovation from Samuel Sternberg’s lab at Columbia University, de... biotechnology CRISPR evoCAST gene editing genetic therapy protein evolution transposase